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- Advances in Nucleic Acid Therapeutics, CHAPTER 6 Splicing Modulation for Therapeutics. Elena Daoutsali, Annemieke Aartsma-Rus
, 2019
, Pages 103-125
- Advances in Nucleic Acid Therapeutics, Foreword
, 2019
, Pages P007-P008
- Advances in Nucleic Acid Therapeutics, CHAPTER 1 History and Development of Nucleotide Analogues in Nucleic Acids Drugs. Sudhir Agrawal, Michael J. Gait
, 2019
, Pages 1-21
- DNA-targeting Molecules as Therapeutic Agents, Chapter 9 Therapeutic Potential of DNA Gene Targeting using Peptide Nucleic Acid (PNA). Peter E. Nielsen
, 2018
, Pages 228-245
- Protein Degradation with New Chemical Modalities: Successful Strategies in Drug Discovery and Chemical Biology, Chapter 14 Classes, Modes of Action and Selection of New Modalities in Drug Discovery. Eric Valeur
, 2020
, Pages 277-316
- Orphan Drugs and Rare Diseases, Chapter 1 Definitions, History and Regulatory Framework for Rare Diseases and Orphan Drugs. David C. Pryde, Stephen C. Groft
, 2014
, Pages 3-31
- Advances in Nucleic Acid Therapeutics, Subject Index
, 2019
, Pages 532-541
- Advances in Nucleic Acid Therapeutics, CHAPTER 2 Mechanisms of Antisense Oligonucleotides. Zhongtian Liu, David R. Corey
, 2019
, Pages 22-31
- Advances in Nucleic Acid Therapeutics, CHAPTER 3 The Medicinal Chemistry of RNase H-activating Antisense Oligonucleotides. Punit P. Seth, Eric E. Swayze
, 2019
, Pages 32-61
- Advances in Nucleic Acid Therapeutics, CHAPTER 9 Oligonucleotide Targeting of Long Non-coding RNAs. I. Blokhin, O. Khorkova, J. Hsiao, C. Wahlestedt
, 2019
, Pages 181-205